Issn  2249-7579
e Issn  2249-7579
Publisher JOURNAL OF PHARMACEUTICAL BIOLOGY
Title

REVIEW ON DEVELOPMENT OF ORPHAN DRUG

Authors
Sai Sujitha G
Sai Sujitha G
Sreekanth Reddy CP
Sreekanth Reddy CP
Jyoshtna Devi K
Jyoshtna Devi K
Jayachandra Reddy P
Jayachandra Reddy P
Keywords
Orphan disease, Regulatory harmonization, Orphan drug. ,

Abstract

A rare disease, also referred to as an "orphan disease", is any disease that affects a small percentage of the population. Most rare diseases are genetic, and thus are present throughout the person's entire life, even if symptoms do not immediately appear. Many rare diseases appear early in life, and about 30 percent of children with rare diseases will die before reaching their fifth birthday. With a single diagnosed patient only, ribose-5-phosphate isomerase deficiency is presently considered the rarest genetic disease. No single cutoff number has been agreed upon for which a disease is considered rare. A disease may be considered rare in one part of the world, or in a particular group of people, but still be common in another.

Volume / Issue / Year

8 , 2 , 2018

Starting Page No / Endling Page No

13 - 16